Journal of Genetic Syndromes & Gene Therapy
Open Access
ISSN: ISSN: 2157-7412
ISSN: ISSN: 2157-7412
Steve Wilton
Steve Wilton
Foundation Chair in Molecular Therapies
Murdoch University
Australia
Steve Wilton is currently working as Foundation Chair in Molecular Therapies, Murdoch University
Australia. His research mainly focusses on Sarepta Therapeutics and the suite of antisense oligomers targeting the dystrophin gene have been licensed through UWA to Sarepta Therapeutics, Cambridge, MA. I am currently extending the therapeutic applications of antisense oligomers to other inherited and acquired conditions including spinal muscular atrophy, cystic fibrosis, multiple sclerosis, Alzheimer’s, Pompe’s disease, congenital muscular dystrophy, Huntington’s and asthma.
Molecular genetics, Antisense oligonucleotide technologies, Gene Therapy, Genetic Therapies, Exon skipping, Splice switching