Articles in press and Articles in process
Commentary
Pages: 1 - 2Marfan Syndrome: Its Causes, Diagnosis and Treatment
DOI: 10.35248/2157-7412.24.15.427
Published Date: 2024-06-13; Received Date: 2023-09-11
Perspective
Pages: 1 - 2CRISPR-Cas9: Transforming Biotechnology in Agriculture Enhancing Crop Durability in Changing Climates
Honghao Li* and Limei Wei
DOI: 10.35248/2157-7412.26.17.484
Published Date: 2026-03-23; Received Date: 2024-06-24
Perspective
Pages: 1 - 2Gene Editing Technologies in Somatic Gene Therapy: Innovations and Challenges
DOI: 10.35248/2157-7412.26.17.485
Published Date: 2026-03-23; Received Date: 2024-10-26
Perspective
Pages: 1 - 2Clinical Guidelines for the Diagnosis and Management of Hemoglobin E/Beta-Thalassemia
DOI: 10.35248/2157-7412.26.17.486
Published Date: 2026-03-23; Received Date: 2024-10-28
Perspective
Pages: 1 - 0Genomic Technologies and their Impact on Autosomal Recessive Disorders
DOI: 10.35248/2157-7412.26.17.487
Published Date: 2026-03-26; Received Date: 2024-10-28
Perspective
Pages: 1 - -1Genomic Technologies and their Impact on Autosomal Dominant Disorders
DOI: 10.35248/2157-7412.26.17.488
Published Date: 2026-03-23; Received Date: 2024-10-28
Perspective
Pages: 1 - 0Sickle Cell Disease and Its Complications: Focus on Acute Chest Syndrome
DOI: 10.35248/2157-7412.26.17.489
Published Date: 2026-03-23; Received Date: 2024-10-28
Perspective
Pages: 1 - 2Targeting Inflammation in Huntington's Disease: Potential Therapeutic Strategies
DOI: 10.35248/2157-7412.26.17.490
Published Date: 2026-03-23; Received Date: 2024-10-28
Perspective
Pages: 1 - 2The Role of UBE3A in Angelman Syndrome: Insights and Therapeutic Opportunities
DOI: 10.35248/2157-7412.26.17.491
Published Date: 2026-03-23; Received Date: 2024-10-28
Commentary
Pages: 1 - 2Allele-Specific Cytosine Base Editing for Retinal Rhodopsin Correction Studies
DOI: 10.35248/2157-7412.26.16.492
Published Date: 2026-03-30; Received Date: 2026-02-27
Short Communication
Pages: 1 - 2RNA-Guided Mitochondrial DNA Editing Approaches for Neuroenergetic Restoration in Leigh Syndrome Models
DOI: 10.35248/2157-7412.26.16.493
Published Date: 2026-03-30; Received Date: 2026-02-27
Commentary
Pages: 1 - 2Precision Splice-Modulating Antisense Oligonucleotide Strategy for Spinal Muscular Atrophy Type II Functional Recovery Assessment
DOI: 10.35248/2157-7412.26.16.494
Published Date: 2026-07-01; Received Date: 2026-06-01
Commentary
Pages: 1 - 2Mitochondrial Genome Correction Approaches in Rare Energy Deficiency Syndromes
DOI: 10.35248/2157-7412.26.16.495
Published Date: 2026-07-01; Received Date: 2026-06-01
Perspective
Pages: 1 - 2Lentiviral Gene Integration Systems in Hematologic Genetic Blood Disorders
DOI: 10.35248/2157-7412.26.16.496
Published Date: 2026-07-01; Received Date: 2026-06-01
Perspective
Pages: 1 - 2Adeno Associated Vector Optimization for Neuromuscular Gene Therapy Disorders
DOI: 10.35248/2157-7412.26.16.497
Published Date: 2026-07-01; Received Date: 2026-06-01
Perspective
Pages: 1 - 2Programmable RNA Editing Systems in Congenital Skeletal Dysplasia Disorders
DOI: 10.35248/2157-7412.26.16.498
Published Date: 2026-07-01; Received Date: 2026-06-01
Commentary
Pages: 1 - 2Long-Term Expression Stability in Adeno-Associated Virus Mediated Gene Delivery for Inherited Metabolic Disorders
DOI: 10.35248/2157-7412.26.16.499
Published Date: 2026-07-01; Received Date: 2026-06-01
Opinion Article
Pages: 1 - 2New Therapeutic Approaches for Rare Inborn Enzyme Deficiencies Using Targeted Gene Delivery Systems
DOI: 10.35248/2157-7412.26.16.500
Published Date: 2026-07-01; Received Date: 2026-06-01
Opinion Article
Pages: 1 - 2Allele-Selective Gene Suppression Strategies in Autosomal Dominant Neurodevelopmental Disorders Using Programmable Molecular Systems
DOI: 10.35248/2157-7412.26.16.501
Published Date: 2026-07-01; Received Date: 2026-06-01
Opinion Article
Pages: 1 - 2CRISPR Mediated Therapeutic Modulation in Pediatric Metabolic Disorders
DOI: 10.35248/2157-7412.26.16.502
Published Date: 2026-07-01; Received Date: 2026-06-01
Short Communication
Pages: 1 - 2RNA Guided Epigenetic Regulation Strategies for Chromosomal Dosage Disorders
DOI: 10.35248/2157-7412.26.16.503
Published Date: 2026-07-01; Received Date: 2026-06-01
Review Article
Pages: 1 - 4Treatment of Autosomal Nonsyndromic Congenital Deafness by AAV Mediated Gene Therapy
Maryam Fatima
Published Date: 2022-05-20; Received Date: 2022-04-15