Epigenetics Research: Open Access
Open Access

Gene Therapy Journals

Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient's cells instead of using drugs or surgeryGene therapy is designed to introduce genetic material into cells to compensate for abnormal genes or to make a beneficial protein. ... Alternately, a sample of the patient's cells can be removed and exposed to the vector in a laboratory setting. The cells containing the vector are then returned to the patientThe goal of gene therapy is to cure or slowdown a genetic disease by repairing the damaged gene responsible for the disease. To achieve this goal, gene therapy requires the technology to insert the missing ? normal? gene into the DNA of the patient?Gene therapy is currently available primarily in a research setting. The U.S. Food and Drug Administration (FDA) has approved only a limited number of gene therapy products for sale in the United States