Journal of Genetic Syndromes & Gene Therapy

Journal of Genetic Syndromes & Gene Therapy
Open Access

ISSN: ISSN: 2157-7412

Volume 17, Issue 2 (2026)

Commentary

Pages: 1 - 2

Precision Splice-Modulating Antisense Oligonucleotide Strategy for Spinal Muscular Atrophy Type II Functional Recovery Assessment

Aarav Nandini Krishnan*

DOI: 10.35248/2157-7412.26.16.494

Share this article

Short Communication

Pages: 1 - 2

RNA Guided Epigenetic Regulation Strategies for Chromosomal Dosage Disorders

Meera Kulkarni*

DOI: 10.35248/2157-7412.26.16.503

Share this article

Opinion Article

Pages: 1 - 2

CRISPR Mediated Therapeutic Modulation in Pediatric Metabolic Disorders

Ananya Iyer*

DOI: 10.35248/2157-7412.26.16.502

Share this article

Opinion Article

Pages: 1 - 2

Allele-Selective Gene Suppression Strategies in Autosomal Dominant Neurodevelopmental Disorders Using Programmable Molecular Systems

Kavita Nai*

DOI: 10.35248/2157-7412.26.16.501

Share this article

Opinion Article

Pages: 1 - 2

New Therapeutic Approaches for Rare Inborn Enzyme Deficiencies Using Targeted Gene Delivery Systems

Arjun Mehta*

DOI: 10.35248/2157-7412.26.16.500

Share this article

Commentary

Pages: 1 - 2

Long-Term Expression Stability in Adeno-Associated Virus Mediated Gene Delivery for Inherited Metabolic Disorders

Arjun Mehta*

DOI: 10.35248/2157-7412.26.16.499

Share this article

Perspective

Pages: 1 - 2

Programmable RNA Editing Systems in Congenital Skeletal Dysplasia Disorders

Kavya Srinivasan*

DOI: 10.35248/2157-7412.26.16.498

Share this article

Perspective

Pages: 1 - 2

Adeno Associated Vector Optimization for Neuromuscular Gene Therapy Disorders

Rakesh Nambiar*

DOI: 10.35248/2157-7412.26.16.497

Share this article

Perspective

Pages: 1 - 2

Lentiviral Gene Integration Systems in Hematologic Genetic Blood Disorders

Suresh Balachandran*

DOI: 10.35248/2157-7412.26.16.496

Share this article

Commentary

Pages: 1 - 2

Mitochondrial Genome Correction Approaches in Rare Energy Deficiency Syndromes

Nandini Rajasekar*

DOI: 10.35248/2157-7412.26.16.495

Share this article
Top